Clinical Trial
Phase 3 Follow-up Study of AAV5-hRKp.RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
Disease
Disease type
Hereditary retinal disease
Retinitis Pigmentosa
Orphan drug recognition
Yes
Patient type
Adult
Children
Inclusion / Exclusion
Funding
Industry
Members involved
Main investigators
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/MG_0650-scaled-e1706086196143-230x230-1.jpg)
Pr Isabelle Audo
France
Others investigators
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/bart_leroy.jpg)
Pr Bart LEROY
Belgium
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/portrait_michael_larsen.jpg)
Pr Michael LARSEN
Denmark
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/MG_0650-scaled-e1706086196143-230x230-1.jpg)
Pr Isabelle Audo
France
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/bacci-230x230.png)
Dr Giacomo Maria Bacci
Italy
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/francesca-simonelli-telethon.png)
Pr Francesca Simonelli
Italy
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/portrait_c_boon.jpg)
Dr Camiel BOON
Netherlands
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/carel-hoyng-1-230x230.jpg)
Pr Carel HOYNG
Netherlands
ERN EYE member investigating site
HCP : Principal investigators
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/AdobeStock_615146071_Editorial_Use_Only-430x160.jpeg)
Ghent University Hospital, Ghent, Belgium
Adress
Corneel Heymanslaan 10
9000 Ghent
Belgium
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/Rigshospitalet_20130427_0004F_8739514693-430x160.jpg)
Rigshospitalet, Copenhagen, Denmark
Adress
Inge Lehmanns Vej 7 Entrance 2, 6. floor Section 2061
2100 Copenhagen
Denmark
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/Quinze-Vingts-CHN03-430x160.jpg)
RÉFÉRET National Hospital of Ophthalmology of Quinze-Vingts, Paris, France
Adress
28 Rue de Charenton
75012 Paris
France
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/REF-Carregi-1-430x160.jpg)
AOU Careggi – AOU Meyer Consortium, Firenze, Italy
Adress
Largo Brambilla 3
50134 Florence
Italy
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/Ospedale_San_Paolo_di_Milano-430x160.jpg)
ASST Santi Paolo e Carlo, Milan, Italy
Adress
Via Antonio di Rudinì, n. 8
20142 Milano MI
Italy
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/home5-430x160.jpg)
AOU Università degli Studi della Campania Luigi Vanvitelli, Napoli, Italy
Adress
Via Santa Maria di Costantinopoli
104, 80138 Napoli NA
Italy
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/Monoblocco_San_Martino-430x160.jpg)
Clinica Oculistica – Ospedale Policlinico San Martino IRCCS, Genova, Italy
Adress
Viale Benedetto XV, 7
16132 Genova GE
Italy
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/amc-building1-398x160.jpg)
Leiden University Medical Center/Academic Medical Center Amsterdam, Netherlands
Adress
Albinusdreef 2
2333 ZA Leiden
Netherlands
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/images-275x160.jpg)
Radboud university medical center, Nijmegen, Netherlands
Adress
Geert Grooteplein Zuid 10
6525 GA Nijmegen
Netherlands