How to contact the center
HCP Center

as part of the Rare Diseases Plan 2006-2011, re-labeling in 2017. OPHTARA is
unique consortium part of ERN-EYE with 5 Paris University Hospital sites: Necker
(Coordinator site), Pitié Salpetrière, HEGP, Cochin and Hôtel Dieu (component sites).
Picture : Celette
Contact
OPHTARA – AP-HP, Hôpital Necker-Enfants Malades, Paris, France
Team

Pr Dominique BREMOND-GIGNAC
France

Dr Alejandra Daruich-Matet
France

Pr Matthieu Robert
France
Clinical trials

Open-label, Single-arm, Multicenter Study to Assess the Safety of Cystadrops® in Pediatric Cystinosis Patients From 6 Months to Less Than 2 Years Old

Study of the efficacy of Befizal® 200mg in the treatment of Leber’s hereditary optic neuropathy

Function of the Pigment Epithelium in Patients With Type 1 Neurofibromatosis (NEF-1)

Interest of Intravitreal Injections of Anti-VEGF as Initial and Adjuvant Treatment in Coats Disease.

A phase II, open-label, efficacy study of daily administration of sodium valproate in patients clinically affected by Wolfram syndrome due to monogenic mutation.

A Non-interventional Study of Clinical Experience in Patients Prescribed Raxone® for the Treatment of Leber’s Hereditary Optic Neuropathy (LHON).

Efficacy, Safety and Pharmacokinetics of 3 Doses of REC 0/0559 Eye Drops for the Treatment of Stage 2 (Moderate) and 3 (Severe) Neurotrophic Keratitis in Adult Patients

An International Prospective Natural History Study in Children With a Type II Collagen Disorder With Short Stature

Genetic Study of Patients Suffering From Congenital Amaurosis of Leber or From an Early Severe Retinal Dystrophy.

Genetic Decryption of Leber Congenital Amaurosis (LCA) in a Large Cohort of Independent Families.