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AUDIOWOLF

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Clinical Trial

2020-004594-43 Completed
AUDIOWOLF

A phase II, open-label, efficacy study of daily administration of sodium valproate in patients clinically affected by Wolfram syndrome due to monogenic mutation.

Phase 2
Interventional

Disease

Disease type

Wolfram

Orphan drug recognition

No

Patient type

Adult

Children

Inclusion / Exclusion

Opening date

26/03/2019

Closing date

31/08/2021

Inclusion criteria :

More

Exclusion criteria :

More

Funding

public

Members involved

Main investigators

Dr Christophe ORSSAUD

Substitute

France

Genetic Diagnostics (TWG6), Low Vision Daily Life and Patients Groups (TWG5), National Integration (TWG9), Neuro-Ophthalmology Rare Diseases (WG2), Registries & Epidemiology (TWG7), Research (TWG8)
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ERN EYE member investigating site

HCP : Principal investigators

OPHTARA – Hôpital Européen Georges Pompidou, Paris, France

Adress

Service d'ophtalmologieBât. Lecourbe - RC149 rue de Sèvres

75 015 Paris

France