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PIGMENT – PDE6A gene therapy for retinitis pigmentosa

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Clinical Trial

NCT04611503 Active, Not recruiting
PIGMENT – PDE6A gene therapy for retinitis pigmentosa

PIGMENT – PDE6A gene therapy for retinitis pigmentosa.

Phase 1/2
Interventional

Disease

Disease type

Retinitis Pigmentosa

Orphan drug recognition

Yes

Patient type

Adult

Children

Inclusion / Exclusion

Opening date

02/07/2019

Closing date

31/07/2023

Inclusion criteria :

More

Exclusion criteria :

More

Funding

national institution

Members involved

Main investigators

Dr Susanne KOHL

Substitute

Germany

Genetic Diagnostics (TWG6), Registries & Epidemiology (TWG7), Research (TWG8), Retinal Rare Eye Diseases (WG1)
Working Group Leader
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Others investigators

Dr Katarina Stingl

Representative

Germany

Low Vision Daily Life and Patients Groups (TWG5), Registries & Epidemiology (TWG7), Research (TWG8), Retinal Rare Eye Diseases (WG1)
Working Group Leader
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ERN EYE member investigating site

HCP : Principal investigators

Centre for Ophthalmology, University Eye Hospital, Tübingen, Germany

Adress

Department für Augenheilkunde Tübingen Forschungsinstitut für Augenheilkunde Elfriede-Aulhorn-Str. 7

72076 Tübingen

Germany