Clinical Trial
Disease
Orphan drug recognition
Yes
Patient type
Adult
Children
Inclusion / Exclusion
Funding
Public
Members involved
Others investigators

Dr Johannes Birtel
Substitute
Germany
CPMS & Digital Medecine (TWG10), Genetic Diagnostics (TWG6), Pediatric Ophthalmology Rare Diseases (WG3), Research (TWG8), Retinal Rare Eye Diseases (WG1)

Pr Martin Spitzer
Representative
Germany
Pediatric Ophthalmology Rare Diseases (WG3), Research (TWG8), Retinal Rare Eye Diseases (WG1)
ERN EYE member investigating site
HCP : Others investigators

Universitätsklinikum Hamburg-Eppendorf, Hamburg, Germany
Adress
Martinistraße 52
20251 Hamburg
Germany