Clinical Trial
NCT03252847 Completed
Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) – Retinitis Pigmentosa GTPase Regulator (RPGR)
An Open Label, Multi-centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-associated Virus Vector (AAV2-.RPGR) for Gene Therapy of Adults and Children With X-linked Retinitis Pigmentosa Owing to Defects in Retinitis Pigmentosa GTPase Regulator (RPGR)
Disease
Disease type
Hereditary retinal disease
Retinitis Pigmentosa
Patient type
Adult
Children
Inclusion / Exclusion
Funding
private
Members involved
Others investigators
ERN EYE member investigating site
HCP : Principal investigators
ASST Santi Paolo e Carlo, Milan, Italy
Adress
Via Antonio di Rudinì, n. 8
20142 Milano MI
Italy