Clinical Trial
Disease
Disease type
Wolfram
Orphan drug recognition
No
Patient type
Adult
Children
Inclusion / Exclusion
Funding
public
Members involved
Main investigators
Others investigators

Dr Christophe ORSSAUD
Substitute
France
Genetic Diagnostics (TWG6), Low Vision Daily Life and Patients Groups (TWG5), National Integration (TWG9), Neuro-Ophthalmology Rare Diseases (WG2), Registries & Epidemiology (TWG7), Research (TWG8)
ERN EYE member investigating site
HCP : Principal investigators

Reference Center Rare Diseases ‘Genetic Sensory Diseases’, MAOLYA, Montpellier, France
Adress
Hôpital Gui de ChauliacService Ophtalmologie80, avenue Augustin Fliche 1er étage, bureau 1414
34 295 Montpellier Cedex 5
France

OPHTARA – Hôpital Européen Georges Pompidou, Paris, France
Adress
Service d'ophtalmologieBât. Lecourbe - RC149 rue de Sèvres
75 015 Paris
France