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Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome

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Clinical Trial

NCT03717909 Active, Not recruiting
Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome
Phase 2/3
Interventional

Disease

Disease type

Wolfram

Orphan drug recognition

No

Patient type

Adult

Children

Inclusion / Exclusion

Opening date

28/12/2018

Closing date

15/11/2024

Inclusion criteria :

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Exclusion criteria :

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Funding

public

Members involved

Main investigators

Pr Isabelle MEUNIER

Representative

France

Retinal Rare Eye Diseases (WG1)
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Others investigators

Dr Christophe ORSSAUD

Substitute

France

Genetic Diagnostics (TWG6), Low Vision Daily Life and Patients Groups (TWG5), National Integration (TWG9), Neuro-Ophthalmology Rare Diseases (WG2), Registries & Epidemiology (TWG7), Research (TWG8)
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ERN EYE member investigating site

HCP : Principal investigators

Reference Center Rare Diseases ‘Genetic Sensory Diseases’, MAOLYA, Montpellier, France

Adress

Hôpital Gui de ChauliacService Ophtalmologie80, avenue Augustin Fliche 1er étage, bureau 1414

34 295 Montpellier Cedex 5

France

OPHTARA – Hôpital Européen Georges Pompidou, Paris, France

Adress

Service d'ophtalmologieBât. Lecourbe - RC149 rue de Sèvres

75 015 Paris

France