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Clinical Trial

NCT03963154 Active, Not recruiting
STREAM

Interventional Study of Implantation of hESC-derived RPE in Patients With RP Due to Monogenic Mutation.

Phase 3
Interventional

Disease

Disease type

Retinitis Pigmentosa

Orphan drug recognition

NA

Patient type

Adult

Children

Inclusion / Exclusion

Opening date

19/08/2019

Closing date

15/12/2026

Inclusion criteria :

More

Exclusion criteria :

More

Funding

other

Members involved

Main investigators

Others investigators

Pr Isabelle Audo

Representative

France

Genetic Diagnostics (TWG6), Low Vision Daily Life and Patients Groups (TWG5), National Integration (TWG9), Neuro-Ophthalmology Rare Diseases (WG2), Pediatric Ophthalmology Rare Diseases (WG3), Registries & Epidemiology (TWG7), Research (TWG8), Retinal Rare Eye Diseases (WG1)
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ERN EYE member investigating site

HCP : Principal investigators