Clinical TrialNCT00643747 Completed Safety Study of RPE65 Gene Therapy to Treat Leber Congenital AmaurosisSafety Study of RPE65 Gene Therapy to Treat Leber Congenital Amaurosis Phase 1/2 Interventional Export PDFDiseaseDisease typeLeber Congenital AmaurosisOrphan drug recognitionNAInclusion / Exclusion Opening date01/01/2007 Closing date01/12/2014Inclusion criteria : MoreExclusion criteria : MoreFundingindustryMembers involvedOthers investigators Dr Axel PETZOLDNetherlands Neuro-Ophthalmology Rare Diseases (WG2), Research (TWG8) See more More Export PDF