Clinical Trial
Disease
Disease type
Stargardt Disease
Orphan drug recognition
NA
Patient type
Adult
Children
Inclusion / Exclusion
Funding
industry
Members involved
Main investigators
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/JAS-SAHEL-230x230-1.jpg)
Pr José-Alain Sahel
France
Genetic Diagnostics (TWG6), Low Vision Daily Life and Patients Groups (TWG5), Neuro-Ophthalmology Rare Diseases (WG2), Pediatric Ophthalmology Rare Diseases (WG3), Registries & Epidemiology (TWG7), Research (TWG8), Retinal Rare Eye Diseases (WG1)
Others investigators
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/MG_0650-scaled-e1706086196143-230x230-1.jpg)
Pr Isabelle Audo
Representative
France
Genetic Diagnostics (TWG6), Low Vision Daily Life and Patients Groups (TWG5), National Integration (TWG9), Neuro-Ophthalmology Rare Diseases (WG2), Pediatric Ophthalmology Rare Diseases (WG3), Registries & Epidemiology (TWG7), Research (TWG8), Retinal Rare Eye Diseases (WG1)
ERN EYE member investigating site
HCP : Principal investigators
![](https://www.ern-eye.eu/wp-content/uploads/sites/2/2023/11/Quinze-Vingts-CHN03-430x160.jpg)
RÉFÉRET National Hospital of Ophthalmology of Quinze-Vingts, Paris, France
Adress
28 Rue de Charenton
75012 Paris
France