Clinical Trial
NCT06591806 Recruiting, Active
An Observational Study in Children and Adults With Stargardt Disease
A Multicenter, Prospective, Longitudinal, Observational Study in Children and Adults With Stargardt Disease Related Atrophy Secondary to Biallelic Mutations in the ABCA4 Gene
Disease
Disease type
Stargardt Disease
Patient type
Adult
Children
Inclusion / Exclusion
Funding
Industry
Members involved
Others investigators

Pr Francesca Simonelli
Representative
Italy
Genetic Diagnostics (TWG6), National Integration (TWG9), Registries & Epidemiology (TWG7), Retinal Rare Eye Diseases (WG1)
ERN EYE member investigating site
HCP : Principal investigators

AOU Università degli Studi della Campania Luigi Vanvitelli, Napoli, Italy
Adress
Via Santa Maria di Costantinopoli
104, 80138 Napoli NA
Italy