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An Observational Study in Children and Adults With Stargardt Disease

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Clinical Trial

NCT06591806 Recruiting, Active
An Observational Study in Children and Adults With Stargardt Disease

A Multicenter, Prospective, Longitudinal, Observational Study in Children and Adults With Stargardt Disease Related Atrophy Secondary to Biallelic Mutations in the ABCA4 Gene

Observational
Observational

Disease

Disease type

Stargardt Disease

Patient type

Adult

Children

Inclusion / Exclusion

Opening date

05/01/2024

Closing date

30/06/2026

Inclusion criteria :

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Exclusion criteria :

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Funding

Industry

Members involved

Others investigators

Pr Francesca Simonelli

Representative

Italy

Genetic Diagnostics (TWG6), National Integration (TWG9), Registries & Epidemiology (TWG7), Retinal Rare Eye Diseases (WG1)
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ERN EYE member investigating site

HCP : Principal investigators