Clinical Trial
Disease
Disease type
Leber Congenital Amaurosis
Orphan drug recognition
No
Inclusion / Exclusion
Opening date
12/12/2017
Closing date
12/12/2018
Funding
industry
Members involved
Main investigators
Pr Michael LARSEN
Representative
Denmark
Neuro-Ophthalmology Rare Diseases (WG2), Research (TWG8), Retinal Rare Eye Diseases (WG1)
Working Group Leader
Others investigators
Line Kessel
Denmark
Genetic Diagnostics (TWG6), Neuro-Ophthalmology Rare Diseases (WG2), Pediatric Ophthalmology Rare Diseases (WG3), Registries & Epidemiology (TWG7), Research (TWG8), Retinal Rare Eye Diseases (WG1)
ERN EYE member investigating site
HCP : Principal investigators
Rigshospitalet, Copenhagen, Denmark
Adress
Inge Lehmanns Vej 7 Entrance 2, 6. floor Section 2061
2100 Copenhagen
Denmark