Biedru informācija
Pr Francesca Simonelli
Itālija
Komanda
Pr Francesco Testa
Itālija
Dr Raffaella Brunetti Pierri
Itālija
Dr Valentina Di Iorio
Itālija
HCP centrs
kontakts
AOU Università degli Studi della Campania Luigi Vanvitelli, Napoli, Italy
Klīniskie izmēģinājumi
An Open-Label, Dose Escalation and Double-Masked, Randomized, Controlled Study to Evaluate the Safety and Tolerability of Sepofarsen in Pediatric Subjects G (p.Cys998X) Mutation.
Phase 3 Randomized, Controlled Study of AAV5-hRKp.RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
Phase 3 Follow-up Study of AAV5-hRKp.RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
Clinical and Molecular Studies in Families With Inherited Eye Disease
Natural history of patients with inherited retinal diseases due to mutations in RPE65 gene
Safety and Efficacy of Emixustat in Stargardt Disease.
Natural History Study in Subjects With Usher Syndrome.
A Phase 2b Randomized, Double-masked, Controlled Trial to Establish the Safety and Efficacy of Zimura™ (Complement C5 Inhibitor) Compared to Sham in Subjects With Autosomal Recessive Stargardt Disease
A Phase 3 Multicenter, Randomized, Double Masked, Sham- Controlled Clinical Trial to Assess the Safety and Efficacy of Intravitreal Administration of Zimura (Complement C5 Inhibitor) in Patients With Geographic Atrophy Secondary to Age-Related Macular Degeneration