Klinikinis tyrimas
Phase 3 Randomized, Controlled Study of AAV5-hRKp.RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
Ligos
Ligos tipas
Paveldima tinklainės liga
Retinitas Pigmentosa
Paciento tipas
Suaugęs
Gynimas
Įtraukimas / išskyrimas
Finansavimas
privatus
Dalyvaujantys nariai
Kiti tyrėjai

Pr Bart LEROY
Belgija

Pr Michael LARSEN
Danija

Pr Isabelle Audo
Prancūzija

Dr Giacomo Maria Bacci
Italija

Pr Francesca Simonelli
Italija

Pr Camiel BOON
Nyderlandai

Pr Carel HOYNG
Nyderlandai
ERN EYE nario tyrimo svetainė
HCP: pagrindiniai tyrėjai

Ghent University Hospital, Ghent, Belgium
Adress
Corneel Heymanslaan 10
9000 Ghent
Belgium

Rigshospitalet, Copenhagen, Denmark
Adress
Inge Lehmanns Vej 7 Entrance 2, 6. floor Section 2061
2100 Copenhagen
Denmark

RÉFÉRET National Hospital of Ophthalmology of Quinze-Vingts, Paris, France
Adress
28 Rue de Charenton
75012 Paris
France

AOU Careggi – AOU Meyer Consortium, Firenze, Italy
Adress
Largo Brambilla 3
50134 Florence
Italy

Clinica Oculistica – Ospedale Policlinico San Martino IRCCS, Genova, Italy
Adress
Viale Benedetto XV, 7
16132 Genova GE
Italy

AOU Università degli Studi della Campania Luigi Vanvitelli, Napoli, Italy
Adress
Via Santa Maria di Costantinopoli
104, 80138 Napoli NA
Italy

ASST Santi Paolo e Carlo, Milan, Italy
Adress
Via Antonio di Rudinì, n. 8
20142 Milano MI
Italy

Amsterdam University Medical Center / Leiden University Medical Center
Adress
Albinusdreef 2
2333 ZA Leiden
Netherlands

Radboud university medical center, Nijmegen, Netherlands
Adress
Geert Grooteplein Zuid 10
6525 GA Nijmegen
Netherlands