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A Long-term Follow-up Study to Evaluate the Safety and efficacy of Retinal Gene Therapy in Subjects with choroideremia treated previously with Adeno-Associated Viral Vector Encoding Rab Escort Protein-1 (AAV2-REP1) in an Antecedent Study.
Status of the trial: Active, Recruiting
Orphan Drug Recognition: Yes
Inclusion: Subjects are willing and able to give informed consent for participation in the study, and have received a sub-retinal injection of AAV2-REP1 for CHM in an antecedent study.
Exclusion: There are no exclusion criteria for this study.
Funder Type: industry
Principal location of the trial
HCP: Principal investigators
HCP: Other investigators