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A double-masked, randomized, controlled, multiple-dose study to evaluate the efficacy, safety, tolerability and systemic exposure of QR-110 in Subjects with Leber’s Congenital Amaurosis (LCA) due to c.2991+1655A>G mutation (p.Cys998X) in the CEP290 gene (Illuminate).
Status of the trial: Active, Not recruiting
Orphan Drug Recognition: No
Funder Type: industry
Principal location of the trial
HCP: Principal investigators
HCP: Other investigators